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901
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Efficacy of Cabozantinib in Metastatic MiT Family Translocation Renal Cell Carcinomas
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Thouvenin, Jonathan;
Alhalabi, Omar;
Carlo, Maria;
Carril-Ajuria, Lucia;
Hirsch, Laure;
Martinez-Chanza, Nieves;
Né
grier, Sylvie;
Campedel, Luca;
Martini, Dylan;
Borchiellini, Delphine;
Chahoud, Jad;
Lodi, Massimo;
Barthé
lé
my, Philippe;
Hasanov, Elshad;
Hahn, Andrew W;
Gil, Thierry;
Viswanathan, Srinivas R;
Bakouny, Ziad;
Msaouel, Pavlos;
Asim Bilen, Mehmet;
Choueiri, Toni K;
Albiges, Laurence;
Tannir, Nizar M;
Malouf, Gabriel G;
MD Anderson Cancer Center (MDACC) , Houston, TX , USA;
Memorial Sloan Kettering Cancer Center , New York, NY , USA;
Institut Gustave Roussy , Villejuif , France;
Dana-Farber Cancer Institute (DFCI) , Boston, MA , USA;
Institut Jules Bordet , Bruxelles , Belgium;
Université
Claude Bernard, Centre Lé
on Bé
rard , Lyon , France;
AP-HP, Groupe hospitalier Pitié
-Salpê
triè
re , Paris , France;
Winship Cancer Institute of Emory University , Atlanta, GA , USA;
Antoine Lacassagne Cancer Center , Nice , France;
Department of Genitourinary Oncology, Moffitt Cancer Center , Tampa, FL , USA;
Institut de Cancé
rologie Strasbourg Europe (ICANS/HUS) , Strasbourg , France;
(The oncologist,
v.27,
2022,
pp.1041-1047)
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902
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Asciminib (ASC) in Combination with Imatinib (IMA), Nilotinib (NIL), or Dasatinib (DAS) May be a Potential Treatment (Tx) Option in Patients (Pts) with Philadelphia Chromosome-Positive Chronic Myeloid Leukemia in Chronic Phase or Accelerated Phase (Ph+ CML-CP/AP): Final Results from the Asciminib Phase 1 Study
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Cortes, Jorge;
Lang, Fabian;
Rea, Delphine;
Hochhaus, Andreas;
Breccia, Massimo;
Goh, Yeow Tee;
Heinrich, Michael C.;
Hughes, Timothy P;
Janssen, Jeroen J.W.M.;
le Coutre, Philipp;
Minami, Hironobu;
Sasaki, Koji;
DeAngelo, Daniel J.;
Sanchez-Olle, Gessami;
Pognan, Nathalie;
Jose, Jomy;
Hoch, Matthias;
Mauro, Michael;
1Georgia Cancer Center, Augusta University, Augusta, GA;
2Hematology/Oncology, Klinikum der Goethe Universitä
t, Frankfurt/Main, Germany;
3Hematology Department, Hô
pital Saint-Louis, Paris, France;
4Universitä
tsklinikum Jena, Jena, Germany;
5Department of Translational and Precision Medicine, Hematology-Sapienza University, Rome, Italy;
6Department of Hematology, Singapore General Hospital, Singapore, Singapore;
7Department of Medicine, Division of Hematology and Oncology, Portland VA Health Care System and Oregon Health & Science University, Knight Cancer Institute, Portland, OR;
8South Australian Health and Medical Research Institute (SAHMRI), Adelaide, Australia;
9Department of Hematology, Amsterdam University Medical Centers, VUmc, Amsterdam, Netherlands;
10Charité
-Universitä
tsmedizin Berlin, Berlin, Germany;
11Department of Medical Oncology and Hematology, Kobe University Hospital, Kobe, Japan;
12Department of Leukemia, The University of Texas;
(Blood,
v.142,
2023,
pp.868-868)
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903
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Asciminib, a First-in-Class STAMP Inhibitor, Provides Durable Molecular Response in Patients (pts) with Chronic Myeloid Leukemia (CML) Harboring the T315I Mutation: Primary Efficacy and Safety Results from a Phase 1 Trial
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Cortes, Jorge E.;
Hughes, Timothy P.;
Mauro, Michael J.;
Hochhaus, Andreas;
Rea, Delphine;
Goh, Yeow Tee;
Janssen, Jeroen;
Steegmann, Juan Luis;
Heinrich, Michael C.;
Talpaz, Moshe;
Etienne, Gabriel;
Breccia, Massimo;
Deininger, Michael W.;
le Coutre, Philipp D;
Lang, Fabian;
Aimone, Paola;
Polydoros, Fotis;
Cacciatore, Silvia;
Stenson, Laura;
Kim, Dong-Wook;
Georgia Cancer Center Augusta University, Augusta, GA;
South Australian Health and Medical Research Institute SAHMRI, Adelaide, Australia;
Myeloproliferative Neoplasms Program, Leukemia Service, Memorial Sloan Kettering Cancer Center, New York, NY;
Klinik fü
r Innere Medizin II, Jena, Germany;
Hopital Saint Louis, Paris, France;
Department of Hematology, Singapore General Hospital, Singapore, Singapore;
VU University Medical Center, Amsterdam, NLD;
Hospital de La Princesa, Madrid, Spain;
Portland VA Health Care System, Portland, OR;
University of Michigan Comprehensive Cancer Center, Ann Arbor, MI;
Hematology Department, Institut Bergonié
, Bordeaux, France;
Department of Translational and Precision Medicine, Sapienza University, Rome, Italy;
Huntsman Cancer Institute, The University of Utah, Salt Lake City, UT;
Charité
- Universitä
tsmedizin Berlin, Berlin, Germany;
Department of Medicine II, Hematology/Oncology, Goethe University, Frankfurt, Germany;
(Blood,
v.136,
2020,
pp.47-50)
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904
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The current role of next-generation DNA sequencing in routine care of patients with hereditary cardiovascular conditions: a viewpoint paper of the European Society of Cardiology working group on myocardial and pericardial diseases and members of the European Society of Human Genetics
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Mogensen, Jens;
van Tintelen, J. Peter;
Fokstuen, Siv;
Elliott, Perry;
van Langen, Irene M.;
Meder, Benjamin;
Richard, Pascale;
Syrris, Petros;
Caforio, Alida L.P.;
Adler, Yehuda;
Anastasakis, Aris;
Gimeno, Juan R.;
Klingel, Karin;
Linhart, Ales;
Imazio, Massimo;
Pinto, Yigal;
Newbery, Ruth;
Schmidtke, Joerg;
Charron, Philippe;
Department of Cardiology, Odense University Hospital, Odense, Denmark;
Department of Clinical Genetics, Academic Medical Center, Amsterdam, The Netherlands;
Genetic Medicine, University Hospitals of Geneva, Switzerland;
The Heart Hospital, University College London Hospitals Trust, London, UK;
Department of Genetics, University Medical Centre Groningen, University of Groningen, the Netherlands;
Department of Internal Medicine III, University of Heidelberg, Germany;
Fonctional Unit of Cardiogenetics and Myogenetics, Hô
pital Pitié
-Salpê
triè
re, Paris, France;
UCL Institute of Cardiovascular Science, London, UK;
Division of Cardiology, Department of Cardiological, Thoracic and Vascular Sciences, University of Padova, Padua, Italy;
Chaim Sheba Medical Center, Tel Hashomer and Sackler University, Tel Aviv, Israel;
Unit of Inherited Cardiovascular Diseases, 1st Department of Cardiology, Athens University Medical School, Athens, Greece;
Department of Cardio;
(European heart journal,
v.36,
2015,
pp.1367-1370)
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905
-
DNA Methylation Profiling in Pheochromocytoma and Paraganglioma Reveals Diagnostic and Prognostic Markers
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de Cubas, Aguirre A.;
Korpershoek, Esther;
Inglada-Pé
rez, Lucia;
Letouzé
, Eric;
Currá
s-Freixes, Maria;
Ferná
ndez, Agustin F.;
Comino-Mé
ndez, Iñ
aki;
Schiavi, Francesca;
Mancikova, Veronika;
Eisenhofer, Graeme;
Mannelli, Massimo;
Opocher, Guiseppe;
Timmers, Henri;
Beuschlein, Felix;
de Krijger, Ronald;
Cascon, Alberto;
Rodrí
guez-Antona, Cristina;
Fraga, Mario F.;
Favier, Judith;
Gimenez-Roqueplo, Anne-Paule;
Robledo, Mercedes;
Hereditary Endocrine Cancer Group, Spanish National Cancer Research Centre (CNIO), Madrid, Spain.;
Department of Pathology, Erasmus MC Cancer Institute, University Medical Center, Rotterdam, the Netherlands.;
Hereditary Endocrine Cancer Group, Spanish National Cancer Research Centre (CNIO), Madrid, Spain.;
Programme Cartes d'Identité
des Tumeurs, Ligue Nationale Contre Le Cancer, Paris, France.;
Hereditary Endocrine Cancer Group, Spanish National Cancer Research Centre (CNIO), Madrid, Spain.;
Cancer Epigenetics Laboratory, Institute of Oncology of Asturias (IUOPA), HUCA, University of Oviedo, Asturias, Spain.;
Hereditary Endocrine Cancer Group, Spanish National Cancer Research Centre (CNIO), Madrid, Spain.;
Familial Cancer Clinic, Veneto Institute of Oncology, Padova, Italy.;
Hereditary Endocrine Cancer Group, Spanish National Cancer Research Centre (CNIO), Madrid, Spain.;
Institute of Clinical Chemistry and Laboratory Medicine, Technische Universitä
t Dresden, Dres;
(Clinical Cancer research : an official journal of the American Association for Cancer Research,
v.21,
2015,
pp.3020-3030)
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906
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The role of autologous stem cell transplantation in patients with nodal peripheral T‐cell lymphomas in first complete remission: Report from COMPLETE, a prospective, multicenter cohort study
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Park, Steven I.;
Horwitz, Steven M.;
Foss, Francine M.;
Pinter‐
Brown, Lauren C.;
Carson, Kenneth R.;
Rosen, Steven T.;
Pro, Barbara;
Hsi, Eric D.;
Federico, Massimo;
Gisselbrecht, Christian;
Schwartz, Marc;
Bellm, Lisa A.;
Acosta, Mark;
Advani, Ranjana H.;
Feldman, Tatyana;
Lechowicz, Mary Jo;
Smith, Sonali M.;
Lansigan, Frederick;
Tulpule, Anil;
Craig, Michael D.;
Greer, John P.;
Kahl, Brad S.;
Leach, Joseph W.;
Morganstein, Neil;
Casulo, Carla;
Shustov, Andrei R.;
Levine Cancer Institute, Charlotte, North Carolina;
Memorial Sloan Kettering Cancer Center, New York, New York;
Yale University, New Haven, Connecticut;
University of California Irvine, Irvine, California;
Washington University School of Medicine, St. Louis, Missouri;
City of Hope, Duarte, California;
Robert H. Lurie Comprehensive Cancer Center, Northwestern University, Chicago, Illinois;
Cleveland Clinic, Cleveland, Ohio;
Centro Oncologico Modenese, Policlinico Modena, Italy;
Saint Louis Hospital, Paris, France;
MS Biostatistics, LLC, Clermont, Florida;
MedNet Solutions, Minnetonka, Minnesota;
Spectrum Pharmaceuticals, Inc, Irvine, California;
Stanford University Medical Center, Stanford, California;
Hackensack University Medical Center, Hackensack, New Jersey;
Emory University, Atlanta, Georgia;
University of Chicago, Chicago, Illinois;
Massachusetts Gene;
(Cancer,
v.125,
2019,
pp.1507-1517)
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907
-
Reduced Intensity Vs. Standard Conditioning Followed By Allogeneic Stem Cell Transplantation for Patients with MDS or Secondary AML: A Prospective, Randomized Phase III Study of the Chronic Malignancies Working Party of the EBMT (RICMAC-Trial)
-
Krö
ger, Nicolaus;
Brand, Ronald;
Niederwieser, Dietger;
Platzbecker, Uwe;
Hü
bel, Kai;
Weber, Thomas;
Robin, Marie;
Stelljes, Matthias;
Afanasiev, Boris V;
Heim, Dominik;
Lambertenghi Deliliers, Giorgio;
Onida, Francesco;
Dreger, Peter;
Pini, Massimo;
Guidi, Stefano;
Volin, Liisa;
Gramatzki, Martin;
Bethge, Wolfgang A.;
Poire, Xavier;
Kobbe, Guido;
van Os, Marleen;
Iacobelli, Simona;
de Witte, Theo;
University Medical Center Hamburg-Eppendorf, Hamburg, Germany;
Leiden University Medical Center, Leiden, Netherlands;
University Hospital Leipzig, Leipzig, Germany;
University Hospital Dresden, Dresden, Germany;
University of Cologne, Cologne, Germany;
University Hospital Halle (Saale), Halle, Germany;
Saint Louis Hospital, Paris, France;
University of Muenster, Muenster, Germany;
BMT Center of St Petersburg Pavlov State Medical University, St Petersburg, Russia;
University Hospital Basel, Basel, Switzerland;
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, University of Milan, Milan, Italy;
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, University of Milan, Milan, Italy;
University of Heidelberg, Heidelberg, Germany;
Hematology and Marrow Transplant, A.O. SS Antonio e Biagio e C. Arrigo, Alessandria-Italy., Alessandria, Italy;
Ospedale di Careggi, Firenze, Italy;
Helsinki University Central Hospital, Department of Medicine, Helsinki, Finland;
Univ;
(Blood,
v.124,
2014,
pp.320-320)
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908
-
The MAGNOLIA Trial: Zanubrutinib, a Next-Generation Bruton Tyrosine Kinase Inhibitor, Demonstrates Safety and Efficacy in Relapsed/Refractory Marginal Zone Lymphoma
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Opat, Stephen;
Tedeschi, Alessandra;
Linton, Kim;
McKay, Pamela;
Hu, Bei;
Chan, Henry;
Jin, Jie;
Sobieraj-Teague, Magdalena;
Zinzani, Pier Luigi;
Coleman, Morton;
Thieblemont, Catherine;
Browett, Peter;
Ke, Xiaoyan;
Sun, Mingyuan;
Marcus, Robert;
Portell, Craig A.;
Ardeshna, Kirit;
Bijou, Fontanet;
Walker, Patricia;
Hawkes, Eliza A.;
Mapp, Sally;
Ho, Shir-Jing;
Talaulikar, Dipti;
Zhou, Ke-Shu;
Co, Melannie;
Li, Xiaotong;
Zhou, Wenxiao;
Cappellini, Massimo;
Tankersley, Chris;
Huang, Jane;
Trotman, Judith;
Monash Health, Monash University, Clayton, Victoria, Australia.;
ASST Grande Ospedale Metropolitano Niguarda, Milan, Italy.;
Division of Cancer Sciences, Faculty of Biology Medicine and Health, University of Manchester, Manchester Cancer Research Centre, Manchester, United Kingdom.;
Beatson West of Scotland Cancer Centre, Glasgow, United Kingdom.;
Levine Cancer Institute University City, Carolinas Medical Center, Atrium Health, Charlotte, North Carolina.;
North Shore Hospital, Auckland, New Zealand.;
The First Affiliated Hospital, School of Medicine, Zhejiang University Hangzhou, Zhejiang, China.;
Flinders Medical Centre, Bedford Park, South Australia, Australia.;
IRCCS Azienda Ospedaliero, Universitaria di Bologna, Bologna, Italy.;
WCM Research Alliance, Weill Cornell Medicine, Lake Success, New York.;
Service d'Hé
matologie-Oncologie, Hô
pital Saint-Louis, APHP, Paris, France.;
Auckland City Hospital, University of Auckland, Grafton, Auckland, New Zealand.;
Pe;
(Clinical Cancer research : an official journal of the American Association for Cancer Research,
v.27,
2021,
pp.6323-6332)
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909
-
Bridging animal and clinical research during SARS-CoV-2 pandemic: A new-old challenge
-
Winkler, Martin S.;
Skirecki, Tomasz;
Brunkhorst, Frank M.;
Cajander, Sara;
Cavaillon, Jean-Marc;
Ferrer, Ricard;
Flohé
, Stefanie B.;
Garcí
a-Salido, Alberto;
Giamarellos-Bourboulis, Evangelos J.;
Girardis, Massimo;
Kox, Matthijs;
Lachmann, Gunnar;
Martin-Loeches, Ignacio;
Netea, Mihai G.;
Spinetti, Thibaud;
Schefold, Joerg C.;
Torres, Antoni;
Uhle, Florian;
Venet, Fabienne;
Weis, Sebastian;
Scherag, André
;
Rubio, Ignacio;
Osuchowski, Marcin F.;
Department of Anesthesiology, Emergency and Intensive Care Medicine, University of Gö
ttingen, Gö
ttingen, Robert-Koch-Str. 40, 37085 Gö
ttingen, Germany;
Laboratory of Flow Cytometry, Centre of Postgraduate Medical Education, Warsaw, Poland;
Dept. of Anesthesiology and Intensive Care Medicine & Center for Sepsis Control and Care (CSCC), Jena University Hospital-Friedrich Schiller University, Am Klinikum 1, 07747 Jena, Germany;
Department of Infectious Diseases, Faculty of Medicine and Health, Ö
rebro University, Sweden;
French National Research Agency (ANR), Paris, France;
Intensive Care Department and Shock, Organ Dysfunction and Resuscitation Research Group, Vall d'Hebron University Hospital, Vall d'Hebron Barcelona Hospital Campus, Passeig Vall d'Hebron 119-129, Barcelona, 08035, Spain;
Department of Trauma, Hand, and Reconstructive Surgery, University Hospital Essen, University Duisburg-Essen, Hufelandstr. 55, 45147 Essen, Germany;
Pediatric Critical Care Un;
(EBioMedicine,
v.66,
2021,
pp.103291)
-
910
-
EXpert consensus On Diaphragm UltraSonography in the critically ill (EXODUS): a Delphi consensus statement on the measurement of diaphragm ultrasound-derived parameters in a critical care setting
-
Haaksma, Mark E.;
Smit, Jasper M.;
Boussuges, Alain;
Demoule, Alexandre;
Dres, Martin;
Ferrari, Giovanni;
Formenti, Paolo;
Goligher, Ewan C.;
Heunks, Leo;
Lim, Endry H. T.;
Mokkink, Lidwine B.;
Soilemezi, Eleni;
Shi, Zhonghua;
Umbrello, Michele;
Vetrugno, Luigi;
Vivier, Emmanuel;
Xu, Lei;
Zambon, Massimo;
Tuinman, Pieter R.;
Department of Intensive Care Medicine, Amsterdam University Medical Centers, location VUmc, Postbox 7507, 1007MB Amsterdam, The Netherlands;
Department of Intensive Care Medicine, Amsterdam University Medical Centers, location VUmc, Postbox 7507, 1007MB Amsterdam, The Netherlands;
Aix Marseille Université
, Center for Cardiovascular and Nutrition Research (C2VN), INSERM, INRAE, and Service d’Explorations Fonctionnelles Respiratoires, CHU Nord, Assistance Publique Des Hô
pitaux de Marseille, Marseille, France;
AP-HP, Groupe Hospitalier Universitaire APHP-Sorbonne Université
, Site Pitié
-Salpê
triè
re, Service de Mé
decine Intensive Et Ré
animation (Dé
partement R3S), and Sorbonne Université
, INSERM, UMRS1158 Neurophysiologie Respiratoire Expé
rimentale Et Clinique, 75005 Paris, France;
AP-HP, Groupe Hospitalier Universitaire APHP-Sorbonne Université
, Site Pitié
-Salpê
triè
re, Service de M&ea;
(Critical care : CC,
v.26,
2022,
pp.99)